The first gene-therapy trial was in 1990, involved a girl...
The first gene-therapy trial was in 1990, involved a girl with an inherited immune deficiency.
Gene therapy involves the insertion of normal genes to replace defective ones.
Early genetic technology involved simple organisms such as bacteria. Scientists inserted genes to produce bacteria with useful new traits.
A cell must first be tricked into accepting foreign DNA. The cell must then incorporate the DNA. It must make the DNA part of its genome.
Another type of gene therapy is used to treat cancer.
The most important factor in the development of gene therapy is the fact that, for genetic disorders, there is only one way of curing the disease – replacing the defective gene with a healthy copy – and therefore gene therapy is the only hope of finding cures for such disorders
the transplantation of normal genes into cells in place of missing or defective ones in order to correct genetic disorders.
The most important factor in the development of gene therapy is the fact that, for genetic disorders, there is only one way of curing the disease – replacing the defective gene with a healthy copy – and therefore gene therapy is the only hope of finding cures for such disorders
pros ... Gene therapy, when successful, can have a number of advantages over drug therapy such as providing a cure rather than easing the symptoms. These advantages are discussed in detail in the section ‘Advantages of Gene Therapy’.
cons ... The current lack of knowledge and understanding of the treatment means that its safety is unknown. The current scientific understanding is based on theory rather than solid fact. This, however, can be improved with further research and practice.
Cons ... In clinical trials already carried out the effects of the treatment have only been short-lived. To achieve long term results much more research is needed.

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